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Gene therapy has tremendous potential for the treatment of neurological disorders. There has been substantial progress in the development of gene therapy strategies for neurological disorders over the last two decades. Gene Therapy in Neurological Disorders thoroughly reviews currently available gene therapy tools and presents examples of their application in a variety of neurological diseases. The book begins with general reviews of gene therapy strategies with a focus on neurological disorders. The remainder of the chapters present approaches to specific neurological disorders. Each chapter gives an in-depth introduction to the relevant field before diving into the specific tool or application. The book aims to help investigators, students and research staff better understand the principles of gene therapy and its application in the nervous system.--
Nervous system --- Nervous System Diseases --- Genetic Therapy --- Gene Expression Regulation. --- Diseases --- Gene therapy. --- therapy. --- methods. --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks --- Organs (Anatomy) --- Neurosciences
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Biologie [Ontwikkelings] --- Biologie du développement --- Development (Biology) --- Developmental biology --- Développement [Biologie du ] --- Genetic regulation --- Genetische regulatie --- Ontwikkelingsbiologie --- Régulation génétique --- Gene Expression Regulation. --- Genes. --- Cistron --- Gene --- Genetic Materials --- Cistrons --- Genetic Material --- Material, Genetic --- Materials, Genetic --- Genome --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks --- Gene Expression Regulation --- Genes
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Emphasizing exciting recent developments in the study of gene structure and transcription processes, this compares and contrasts euykaryotic and prokaryotic gene structure, transcription apparatus and regulation of transcription at molecular level.
Genetic transcription --- Transcription, Genetic --- Transcription génétique --- Genetic transcription. --- Gene Expression Regulation --- Genetic Transcription --- DNA, Ribosomal --- Antisense Elements (Genetics) --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks --- Transcription (Genetics) --- Genetic code --- Organisms --- Genes
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Genetic regulation --- Systems biology --- Gene Expression Regulation. --- Systems Biology. --- Genetic regulation. --- Systems biology. --- Genetics & Genomics. --- Computational biology --- Bioinformatics --- Biological systems --- Molecular biology --- Gene expression --- Gene regulation --- Biosynthesis --- Cellular control mechanisms --- Molecular genetics --- Biology, Systems --- Systems Theory --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks --- Gene expression regulation --- Regulation --- Life Sciences --- Biology
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Immunoglobulin genes --- Genes, Immunoglobulin --- Gene Expression Regulation --- Gene Expression Regulation. --- Genes, Immunoglobulin. --- Antibody genes --- Ig genes --- Ir genes --- Genes, Ig --- Immunoglobulin Genes --- Gene, Ig --- Gene, Immunoglobulin --- Ig Gene --- Ig Genes --- Immunoglobulin Gene --- Immunoglobulin Allotypes --- Immunoglobulin Gm Allotypes --- Immunoglobulin Joining Region --- Gene Rearrangement --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks
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Proteins --- isolation & purification --- periodicals --- Purification --- Biotechnology --- Gene Expression Regulation. --- Proteins. --- Protéines --- isolation & purification. --- Biotechnologie --- Biotechnology. --- Purification. --- Gene Expression Regulation --- Gene Products, Protein --- Gene Proteins --- Protein Gene Products --- Proteins, Gene --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- Proteids --- Molecular Mechanisms of Pharmacological Action --- RNAi Therapeutics --- Gene Regulatory Networks --- Biomolecules --- Polypeptides --- Proteomics --- periodicals. --- Protein --- Protéines
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Gene expression --- Genetic regulation --- Liver cells --- Liver --- Gene Expression Regulation --- Liver Neoplasms --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks --- Abdomen --- Biliary tract --- Hepatic cells --- Hepatocytes --- Cells --- Congresses --- Metabolism&delete& --- Regulation&delete& --- etiology --- cytology --- Human histology. Human cytology --- Human genetics --- Gastroenterology --- Metabolism --- Regulation
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Human genetics --- Molecular biology --- Genetics --- Epigenesis, Genetic. --- Gene Expression Regulation. --- Epigenesis --- Gene expression --- Epigénèse --- Expression génique --- Genetic regulation. --- Gene expression regulation --- Gene regulation --- Biosynthesis --- Cellular control mechanisms --- Molecular genetics --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks --- Epigenetic Process --- Epigenetics Processes --- Epigenetic Processes --- Genetic Epigenesis --- Process, Epigenetic --- Processes, Epigenetic --- Processes, Epigenetics --- DNA Methylation --- Regulation --- Epigénèse --- Expression génique --- Epigenome --- Genetic regulation --- Epigenesis, Genetic --- Gene Expression Regulation
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Gene Expression Regulation. --- Molecular Biology. --- Plant gene expression --- Plant genomes --- Plant molecular genetics --- Molecular genetics --- Plant genetics --- Plant molecular biology --- Plant genome --- Genomes --- Gene expression --- Biochemical Genetics --- Biology, Molecular --- Genetics, Biochemical --- Genetics, Molecular --- Molecular Genetics --- Biochemical Genetic --- Genetic, Biochemical --- Genetic, Molecular --- Molecular Genetic --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks --- Genetic Phenomena --- Gene Expression Regulation --- Molecular Biology
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DNA, Antisense --- Gene Expression Regulation --- RNA, Antisense --- Antisense nucleic acids --- Acides nucléiques antisens --- DNA, Antisense. --- Gene Expression Regulation. --- RNA, Antisense. --- Antisense nucleotides --- Nucleic acids --- Anti-Sense RNA --- Antisense RNA --- Anti Sense RNA --- RNA, Anti-Sense --- Expression Regulation, Gene --- Regulation, Gene Action --- Regulation, Gene Expression --- Gene Action Regulation --- Regulation of Gene Expression --- RNAi Therapeutics --- Gene Regulatory Networks --- Anti-Sense DNA --- Antisense DNA --- Anti Sense DNA --- DNA, Anti-Sense --- Antisense nucleic acids. --- Dna, antisense. --- Gene expression regulation. --- Rna, antisense. --- Acides nucléiques antisens
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